Nonclinical precedent Request an invite
Longest pivotal study
39 weeks
“The nonclinical package submitted to the NDA included general toxicology studies of up to 26 and 39 weeks' duration in mouse (subcutaneous [SC]) and monkey (intrathecal lumbar [ITL]), respectively”
✓ VerifiedFDA integrated review, p. 74Source ↗
Pivotal GLP studies
Juvenile monkey 9-month ITL Q4W; juvenile mouse 13-week ICV Q6W; juvenile mouse 26-week SC Q2W
“In nonclinical toxicology studies, zilganersen was administered via ICV injection in juvenile C57BL/B6Ncrl mouse (13 weeks; 0, 0.05, 0.1, or 0.2 mg every 6 weeks) and via ITL injection in juvenile monkey (9 months; 0, 3, 8, or 25 mg Q4W).”
✓ VerifiedFDA integrated review, p. 74Source ↗
Route in tox
Intrathecal lumbar (monkey), intracerebroventricular and subcutaneous (mouse)
“In nonclinical toxicology studies, zilganersen was administered via ICV injection in juvenile C57BL/B6Ncrl mouse”
✓ VerifiedFDA integrated review, p. 74Source ↗

Email me this as a cited memo

Study length for Zanvastro, each with the regulator's own words, the page and a link. Ready to paste into a briefing document or send to your team.

Same question, other oligonucleotides

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Rytelo

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Spinraza

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Tegsedi

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39 weeks

Viltepso

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Wainua

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Waylivra

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Not stated in public reviews

Summary across all 27 oligonucleotides →