| Amondys 45casimersen · DMD exon 45 (PMO) |
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→ |
| Amvuttravutrisiran · TTR (siRNA) |
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→ |
| Dawnzeradonidalorsen · Prekallikrein / KLKB1 (ASO) |
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→ |
| Defiteliodefibrotide · Fragmented DNA oligonucleotides |
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→ |
| Exondys 51eteplirsen · DMD exon 51 (PMO) |
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→ |
| Givlaarigivosiran · ALAS1 (siRNA) |
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→ |
| Hibsagobepirovirsen · HBV RNA (ASO) |
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→ |
| Izervayavacincaptad pegol · C5 (aptamer) |
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→ |
| Kynamromipomersen · APOB (ASO) |
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→ |
| Leqvioinclisiran · PCSK9 (siRNA) |
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→ |
| Macugenpegaptanib · VEGF-165 (aptamer) |
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→ |
| Onpattropatisiran · TTR (siRNA) |
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→ |
| Oxlumolumasiran · HAO1 (siRNA) |
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→ |
| Qalsodytofersen · SOD1 (ASO) |
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→ |
| Qfitliafitusiran · Antithrombin / SERPINC1 (siRNA) |
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→ |
| Redemploplozasiran · APOC3 (siRNA) |
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→ |
| Rivflozanedosiran · LDHA (siRNA) |
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→ |
| Ryteloimetelstat · Telomerase (oligo) |
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→ |
| Spinrazanusinersen · SMN2 (ASO) |
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→ |
| Tegsediinotersen · TTR (ASO) |
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→ |
| Tryngolzaolezarsen · APOC3 (ASO) |
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→ |
| Viltepsoviltolarsen · DMD exon 53 (PMO) |
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→ |
| Vitravenefomivirsen · CMV IE2 mRNA (ASO) |
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→ |
| Vyondys 53golodirsen · DMD exon 53 (PMO) |
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→ |
| Wainuaeplontersen · TTR (ASO) |
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→ |
| Waylivravolanesorsen · APOC3 (ASO) |
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→ |
| Zanvastrozilganersen · GFAP (ASO) |
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→ |